Ert: Clinical Trials

2 trials of Ert, newest first

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2 terminated. 2 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 22Terminated 2

Follow Ert: new trials by email Literature Review of Ert trials Research Report on Ert

Trials (filtered) newest first · largest first

All 2 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Efficacy and Safety Study of BMN 110 for Morquio A Syndrome Patients Who Have Limited Ambulation
BMN 110 - Mucopolysaccharidosis IVA, Morquio A Syndrome
Phase 2TerminatedBioMarin Pharmaceutical162012-08-012016-01-12
Safety and Exercise Study of Two Doses of BMN 110 for Morquio A Syndrome
BMN 110 - Mucopolysaccharidosis IVA, Morquio A Syndrome
Phase 2TerminatedBioMarin Pharmaceutical252012-04-012016-02-01

Conditions studied

Lysosomal Storage Diseases (2)  ·  Mucopolysaccharidosis IV (2)

Sponsors

BioMarin Pharmaceutical (2)

Countries

Germany (2)  ·  United Kingdom (2)  ·  United States (2)  ·  Canada (1)

Top investigators

Adam Shaywitz, MD PhD (1)  ·  Celeste Decker, M.D. (1)

Results publications

PMID 29159458