2 completed. 2 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 2 | 2 | Completed 2 |
Follow Ert: new trials by email Literature Review of Ert trials Research Report on Ert
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Study of BMN 110 in Pediatric Patients < 5 Years of Age With Mucopolysaccharidosis IVA (Morquio A Syndrome) BMN 110 - Mucopolysaccharidosis IVA, Morquio A Syndrome | Phase 2 | Completed | BioMarin Pharmaceutical | 15 | 2011-10-01 | 2017-08-10 |
| Stem Cell Transplant w/Laronidase for Hurler Stem Cell Transplant, Laronidase ERT - Mucopolysaccharidosis I, Hurler Syndrome | Phase 2 | Completed | Masonic Cancer Center, University of Minnesota | 25 | 2004-03-01 | 2019-07-11 |
Lysosomal Storage Diseases (1) · Metabolism, Inborn Errors (1) · Mucopolysaccharidosis I (1) · Mucopolysaccharidosis IV (1)
BioMarin Pharmaceutical (1) · Masonic Cancer Center, University of Minnesota (1)
United States (2) · Italy (1) · Taiwan (1) · United Kingdom (1)
Debra Lounsbury (1) · Paul Orchard, MD (1)