CTX460: Clinical Trials

1 trial of CTX460, newest first

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1 not yet recruiting. 1 Phase 1, 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 11Not yet recruiting 1
Phase 21Not yet recruiting 1

Follow CTX460: new trials by email Literature Review of CTX460 trials Research Report on CTX460

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
A Trial Evaluating the Safety, Tolerability, Pharmacokinetics, Pharmacodynamics, and Efficacy of CTX460 in Adults With Emphysema Associated With Severe Alpha-1 Antitrypsin Deficiency (AATD)
CTX460 - Alpha-1 Antitrypsin Deficiency (AATD)
Phase 1 / Phase 2Not yet recruitingCRISPR Therapeutics682026-10-312026-09-30

Conditions studied

alpha 1-Antitrypsin Deficiency (1)

Sponsors

CRISPR Therapeutics (1)