Cholic Acids: Clinical Trials

1 trial of Cholic Acids, newest first

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1 completed. 1 Phase 3.

By phase and status

PhaseTrialsStatus
Phase 31Completed 1

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Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Compassionate Treatment of Patients With Inborn Errors of Bile Acid Metabolism With Cholic Acid
Cholic Acids - Infantile Refsum's Disease, Zellweger Syndrome
Phase 3CompletedMirum Pharmaceuticals, Inc.851992-01-012023-10-03

Conditions studied

Adrenoleukodystrophy (1)  ·  Cholestasis (1)  ·  Peroxisomal Disorders (1)  ·  Refsum Disease, Infantile (1)  ·  Zellweger Syndrome (1)

Sponsors

Mirum Pharmaceuticals, Inc. (1)

Countries

United States (1)

Top investigators

James Heubi, MD (1)  ·  Kenneth Setchell, PhD (1)

Results publications

PMID 28644367