AAV5-RPGR: Clinical Trials

1 trial of AAV5-RPGR, newest first

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1 completed. 1 Phase 1, 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 11Completed 1
Phase 21Completed 1

Follow AAV5-RPGR: new trials by email Literature Review of AAV5-RPGR trials Research Report on AAV5-RPGR

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Gene Therapy for X-linked Retinitis Pigmentosa (XLRP) - Retinitis Pigmentosa GTPase Regulator (RPGR)
AAV5-RPGR - X-Linked Retinitis Pigmentosa
Phase 1 / Phase 2CompletedMeiraGTx UK II Ltd492017-07-312025-01-08

Sponsors

MeiraGTx UK II Ltd (1)

Countries

United Kingdom (1)  ·  United States (1)

Top investigators

James Bainbridge, Prof (1)

Results publications

PMID 38871269