1 completed. 1 Phase 1, 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 1 | Completed 1 |
| Phase 2 | 1 | Completed 1 |
Follow AAV5-RPGR: new trials by email Literature Review of AAV5-RPGR trials Research Report on AAV5-RPGR
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Gene Therapy for X-linked Retinitis Pigmentosa (XLRP) - Retinitis Pigmentosa GTPase Regulator (RPGR) AAV5-RPGR - X-Linked Retinitis Pigmentosa | Phase 1 / Phase 2 | Completed | MeiraGTx UK II Ltd | 49 | 2017-07-31 | 2025-01-08 |
United Kingdom (1) · United States (1)