VLCAD deficiency: Clinical Trials

1 trial for VLCAD deficiency, newest first

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1 terminated. 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 21Terminated 1

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Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Phase 2 Study of EPI-743 in Children With Pearson Syndrome
EPI-743 - Pearson Syndrome
Phase 2TerminatedEdison Pharmaceuticals Inc22014-08-312020-11-18

Narrower conditions

Mitochondrial Diseases (1)

Broader conditions

Metabolic Diseases (1)  ·  Nutritional and Metabolic Diseases (1)

Interventions

alpha-tocotrienol quinone (1)

Sponsors

Edison Pharmaceuticals Inc (1)

Countries

United States (1)

Top investigators

Matthew Klein, MD, FACS (1)