1 not yet recruiting, 1 recruiting. .
Follow Sanfilippo Syndrome Type C: new trials by email Literature Review of Sanfilippo Syndrome Type C trials Research Report on Sanfilippo Syndrome Type C
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Natural History to Assess Disease in Patients With MPS IIIC Sanfilippo Syndrome Type C, Mucopolysaccharidosis (MPS) IIIC | Not yet recruiting | Phoenix Nest | 35 | 2026-11-01 | 2026-07-17 | |
| Natural History Study of Participants With Sanfilippo Syndrome Type IIIC Sanfilippo Syndrome Type C | Recruiting | Phoenix Nest | 30 | 2024-11-10 | 2026-05-12 |
Mucopolysaccharidosis III (2) · Mucopolysaccharidoses (1)
Carbohydrate Metabolism, Inborn Errors (2) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2) · Connective Tissue Diseases (2) · Genetic Diseases, Inborn (2) · Lysosomal Storage Diseases (2) · Metabolic Diseases (2) · Metabolism, Inborn Errors (2) · Mucinoses (2) · Nutritional and Metabolic Diseases (2) · Skin and Connective Tissue Diseases (2) · Mucopolysaccharidoses (1)
Phoenix Nest (2)
United States (2) · France (1)