Propionic Acidemia: Clinical Trials

1 trial for Propionic Acidemia, newest first

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1 completed. 1 Phase 3.

By phase and status

PhaseTrialsStatus
Phase 31Completed 1

Follow Propionic Acidemia: new trials by email Literature Review of Propionic Acidemia trials Research Report on Propionic Acidemia

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Carglumic Acid in Methylmalonic Acidemia and Propionic Acidemia
Carglumic Acid - Propionic Acidemia, Methylmalonic Acidemia
Phase 3CompletedKing Abdullah International Medical Research Center332015-11-012019-04-25

Narrower conditions

Methylmalonic acidemia (1)

Broader conditions

Amino Acid Metabolism, Inborn Errors (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Genetic Diseases, Inborn (1)  ·  Metabolic Diseases (1)  ·  Metabolism, Inborn Errors (1)  ·  Nutritional and Metabolic Diseases (1)

Interventions

carglumic acid (1)

Sponsors

King Abdullah International Medical Research Center (1)

Countries

Saudi Arabia (1)

Top investigators

Majid A. Alfadhel, MD (1)

Results publications

PMID 31196016