1 completed. 1 Phase 3.
| Phase | Trials | Status |
|---|---|---|
| Phase 3 | 1 | Completed 1 |
Follow Propionic Acidemia: new trials by email Literature Review of Propionic Acidemia trials Research Report on Propionic Acidemia
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Carglumic Acid in Methylmalonic Acidemia and Propionic Acidemia Carglumic Acid - Propionic Acidemia, Methylmalonic Acidemia | Phase 3 | Completed | King Abdullah International Medical Research Center | 33 | 2015-11-01 | 2019-04-25 |
Amino Acid Metabolism, Inborn Errors (1) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Genetic Diseases, Inborn (1) · Metabolic Diseases (1) · Metabolism, Inborn Errors (1) · Nutritional and Metabolic Diseases (1)
carglumic acid (1)
King Abdullah International Medical Research Center (1)
Saudi Arabia (1)