1 suspended. 1 Phase 1, 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 1 | Suspended 1 |
| Phase 2 | 1 | Suspended 1 |
Follow Mucinoses: new trials by email Literature Review of Mucinoses trials Research Report on Mucinoses
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| RGX-111 Gene Therapy in Patients With MPS I RGX-111 - Mucopolysaccharidosis Type I (MPS I), Hurler Syndrome | Phase 1 / Phase 2 | Suspended | REGENXBIO Inc. | 21 | 2019-04-03 | 2026-03-12 |
Carbohydrate Metabolism, Inborn Errors (1) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Connective Tissue Diseases (1) · Genetic Diseases, Inborn (1) · Lysosomal Storage Diseases (1) · Metabolic Diseases (1) · Metabolism, Inborn Errors (1) · Mucopolysaccharidoses (1) · Nutritional and Metabolic Diseases (1) · Skin and Connective Tissue Diseases (1)
REGENXBIO Inc. (1)
Brazil (1) · United States (1)