Molybdenum Cofactor Deficiency, Complementation Group A: Clinical Trials

1 trial for Molybdenum Cofactor Deficiency, Complementation Group A, newest first

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1 completed. 1 Phase 2, 1 Phase 3.

By phase and status

PhaseTrialsStatus
Phase 21Completed 1
Phase 31Completed 1

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Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Study of ORGN001 (Formerly ALXN1101) in Neonates, Infants and Children With Molybdenum Cofactor Deficiency (MOCD) Type A
ORGN001 (formerly ALXN1101) - Molybdenum Cofactor Deficiency, Type A
Phase 2 / Phase 3CompletedOrigin Biosciences52016-05-012023-10-17

Narrower conditions

Molybdenum cofactor deficiency (1)

Sponsors

Origin Biosciences (1)

Countries

Israel (1)  ·  Norway (1)  ·  Spain (1)  ·  Turkey (Türkiye) (1)  ·  United Kingdom (1)  ·  United States (1)

Top investigators

Liza Squires, M.D. (1)