Hyperoxaluria: Clinical Trials

1 trial for Hyperoxaluria, newest first

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1 active not recruiting. 1 Phase 3.

By phase and status

PhaseTrialsStatus
Phase 31Active not recruiting 1

Follow Hyperoxaluria: new trials by email Literature Review of Hyperoxaluria trials Research Report on Hyperoxaluria

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Long Term Extension Study in Patients With Primary Hyperoxaluria
DCR-PHXC - Primary Hyperoxaluria Type 1 (PH1), Primary Hyperoxaluria Type 2 (PH2)
Phase 3Active not recruitingDicerna Pharmaceuticals, Inc., a Novo Nordisk company752019-07-092026-10-08

Narrower conditions

Genetic Diseases, Inborn (1)  ·  Hyperoxaluria, Primary (1)  ·  Kidney Diseases (1)  ·  Primary hyperoxaluria type 1 (1)  ·  Primary hyperoxaluria type 2 (1)  ·  Urologic Diseases (1)

Broader conditions

Carbohydrate Metabolism, Inborn Errors (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Female Urogenital Diseases (1)  ·  Female Urogenital Diseases and Pregnancy Complications (1)  ·  Male Urogenital Diseases (1)  ·  Metabolic Diseases (1)  ·  Metabolism, Inborn Errors (1)  ·  Nutritional and Metabolic Diseases (1)  ·  Urogenital Diseases (1)

Interventions

nedosiran (1)

Sponsors

Dicerna Pharmaceuticals, Inc., a Novo Nordisk company (1)

Countries

Australia (1)  ·  Canada (1)  ·  France (1)  ·  Germany (1)  ·  Italy (1)  ·  Japan (1)  ·  Lebanon (1)  ·  Netherlands (1)  ·  Norway (1)  ·  Spain (1)  ·  Turkey (Türkiye) (1)  ·  United Kingdom (1)  ·  United States (1)

Top investigators

Verity Rawson, MB.CHB (1)

Results publications

PMID 40193200, PMID 40601241