Dysferlinopathy: Clinical Trials

1 trial for Dysferlinopathy, newest first

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1 terminated. 1 Phase 1.

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PhaseTrialsStatus
Phase 11Terminated 1

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Trials (filtered) newest first · largest first

All 1 trial

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TrialPhaseStatusSponsorEnrollmentStartUpdated
Proteasomal Inhibition for Patients With Mis-sense Mutated Dysferlin
Bortezomib - Dysferlinopathy
Phase 1TerminatedUniversity Hospital, Basel, Switzerland32012-12-012017-09-21

Interventions

Bortezomib (1)

Sponsors

University Hospital, Basel, Switzerland (1)

Countries

Switzerland (1)

Top investigators

Michael Sinnreich, Prof. Dr. MD (1)

Results publications

PMID 22174839, PMID 22318734, PMID 22736764