1 completed, 1 recruiting, 1 unknown, 1 withdrawn. 1 Not applicable, 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Not applicable | 1 | Unknown 1 |
| Phase 2 | 1 | Completed 1 |
Follow Glycogen Storage Disease Type IV: new trials by email Literature Review of Glycogen Storage Disease Type IV trials Research Report on Glycogen Storage Disease Type IV
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Biomarker for Glycogen Storage Diseases (BioGlycogen) Fructose Metabolism, Inborn Errors, Glycogen Storage Disease | Withdrawn | CENTOGENE GmbH Rostock | 2018-08-20 | 2023-02-13 | ||
| Fat and Sugar Metabolism During Exercise in Patients With Metabolic Myopathy Sugar - Metabolism, Inborn Errors, Lipid Metabolism, Inborn Errors | Not applicable | Unknown | Copenhagen University Hospital, Rigshospitalet | 60 | 2016-01-01 | 2019-10-16 |
| GBE Deficiency (GSD IV and APBD) Natural History Study No intervention - Glycogen Storage Disease Type IV, Adult Polyglucosan Body Disease | Recruiting | Duke University | 200 | 2015-12-01 | 2026-05-05 | |
| Triheptanoin Treatment Trial for Patients With Adult Polyglucosan Body Disease Triheptanoin, Vegetable Oil - Adult Polyglucosan Body Disease, Glycogen Brancher Enzyme Deficiency | Phase 2 | Completed | Baylor Research Institute | 23 | 2009-06-01 | 2018-03-05 |
Glycogen Storage Disease Type II (2) · Glycogen Storage Disease Type III (2) · Glycogen Storage Disease Type V (2) · Glycogen Storage Disease Type VII (2) · Polyglucosan Body Disease, Adult Form (2) · Carbohydrate Metabolism, Inborn Errors (1) · Carnitine palmitoyl transferase 2 deficiency (1) · Chanarin-Dorfman Syndrome (1) · Dimauro disease (1) · Fructose Metabolism, Inborn Errors (1) · Glycogen Storage Disease (1) · Glycogen Storage Disease Type I (1) · Glycogen Storage Disease Type Ix (1) · Glycogen Storage Disease Type VI (1)
Congenital, Hereditary, and Neonatal Diseases and Abnormalities (4) · Genetic Diseases, Inborn (4) · Nutritional and Metabolic Diseases (4) · Carbohydrate Metabolism, Inborn Errors (3) · Glycogen Storage Disease (3) · Metabolic Diseases (3) · Metabolism, Inborn Errors (3) · Brain Diseases (2) · Brain Diseases, Metabolic (2) · Brain Diseases, Metabolic, Inborn (2) · Central Nervous System Diseases (2) · Lysosomal Storage Diseases, Nervous System (2) · Muscular Diseases (2) · Muscular Disorders, Atrophic (2) · Muscular Dystrophies (2)
Plant Oils (1) · Sugars (1) · triheptanoin (1)
Baylor Research Institute (1) · CENTOGENE GmbH Rostock (1) · Copenhagen University Hospital, Rigshospitalet (1) · Duke University (1)
Denmark (1) · France (1) · Germany (1) · India (1) · Sri Lanka (1) · United States (1)
Karen L Madsen, MD (1) · Peter Bauer, Prof. (1) · Priya Kishnani, MD (1) · Raphael Schiffmann, M.D, M.H.Sc (1)